LW

Li Weibo Institute for Rare Diseases Research

The Li Weibo Institute for Rare Diseases Research, based in Worcester, MA, specializes in developing therapies for rare diseases such as ALS, Cystic Fibrosis, and Huntington's. Affiliated with UMass Medical School, it advances treatment options for conditions like Alpha-1 and Tay-Sachs, demonstrating focused expertise in rare disease research and therapeutic discovery.



































Li Weibo Institute for Rare Diseases Research | Tilt